What to watch for with gene therapy
"Gene Therapy Is Nearing a Major Breakthrough: Therapies that replace faulty genes with healthy ones to cure deadly diseases are generating exciting lab results. How to invest in a hot sector," by Barron's Andrew Barry:
"The goal of replacement gene therapy is to replace faulty genes with normal ones, in the hope of producing significant benefits or even cures. The process involves packaging healthy genes into neutered viruses, ... which then act as vectors delivered in a single dose either into the bloodstream or .. where the disease is."