New drug for rare pediatric disease will cost $702k per year
David Duprey / AP
The FDA approved Brineura on Thursday, the first drug to treat a rare, fatal nervous system disorder called Batten disease that affects children. BioMarin Pharmaceutical makes the so-called orphan drug and will charge $27,000 for treatment every two weeks, or $702,000 per year, executives said Thursday. That does not include discounts from Medicaid or other discount programs.
That's a huge price tag, but that's not all: BioMarin secured another priority review voucher, which allows a company to get a speedier drug review from the FDA. BioMarin sold its first voucher in 2014 for $67.5 million.